Total submissions: 2
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Labcorp Genetics |
RCV003105618 | SCV003792425 | pathogenic | Charcot-Marie-Tooth disease type 4A | 2023-09-08 | criteria provided, single submitter | clinical testing | This variant is present in population databases (no rsID available, gnomAD 0.003%). For these reasons, this variant has been classified as Pathogenic. ClinVar contains an entry for this variant (Variation ID: 2423924). Disruption of the initiator codon has been observed in individuals with autosomal recessive Charcot-Marie-Tooth disease (PMID: 29184355, 33179230). It has also been observed to segregate with disease in related individuals. This sequence change affects the initiator methionine of the GDAP1 mRNA. The next in-frame methionine is located at codon 69. |
Fulgent Genetics, |
RCV005047425 | SCV005679114 | pathogenic | Charcot-Marie-Tooth disease axonal type 2K; Charcot-Marie-Tooth disease type 4A; Charcot-Marie-Tooth disease, axonal, with vocal cord paresis, autosomal recessive; Charcot-Marie-Tooth disease recessive intermediate A | 2024-04-10 | criteria provided, single submitter | clinical testing |