Total submissions: 1
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Labcorp Genetics |
RCV001975056 | SCV002246068 | pathogenic | 3-methylcrotonyl-CoA carboxylase 1 deficiency | 2021-09-24 | criteria provided, single submitter | clinical testing | For these reasons, this variant has been classified as Pathogenic. This premature translational stop signal has been observed in individual(s) with a positive newborn screening result for MCCC1-related disease although a second variant was not observed (PMID: 22264772). This variant is not present in population databases (ExAC no frequency). This sequence change creates a premature translational stop signal (p.Gln445*) in the MCCC1 gene. It is expected to result in an absent or disrupted protein product. Loss-of-function variants in MCCC1 are known to be pathogenic (PMID: 11181649, 15359379, 22642865). |