Total submissions: 4
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Labcorp Genetics |
RCV000552083 | SCV000634116 | pathogenic | Familial infantile myasthenia | 2024-01-03 | criteria provided, single submitter | clinical testing | This sequence change creates a premature translational stop signal (p.Arg548*) in the CHAT gene. It is expected to result in an absent or disrupted protein product. Loss-of-function variants in CHAT are known to be pathogenic (PMID: 12548525, 21786365, 23292760). This variant is present in population databases (rs369251527, gnomAD 0.005%). This premature translational stop signal has been observed in individual(s) with congenital myasthenic syndrome (PMID: 12548525, 29189923). ClinVar contains an entry for this variant (Variation ID: 461449). For these reasons, this variant has been classified as Pathogenic. |
Women's Health and Genetics/Laboratory Corporation of America, |
RCV003155228 | SCV003844879 | pathogenic | Congenital myasthenic syndrome | 2023-02-16 | criteria provided, single submitter | clinical testing | Variant summary: CHAT c.1642C>T (p.Arg548X) results in a premature termination codon, predicted to cause a truncation of the encoded protein or absence of the protein due to nonsense mediated decay, which are commonly known mechanisms for disease. Truncations downstream of this position have been cited as pathogenic and disease-associated in ClinVar and HGMD. The variant allele was found at a frequency of 1.6e-05 in 251368 control chromosomes (gnomAD). c.1642C>T has been reported in the literature in individuals affected with Congenital Myasthenic Syndrome (e.g. Maselli_2003, McMacken_2018). One clinical diagnostic laboratory has submitted clinical-significance assessments for this variant to ClinVar after 2014 and classified the variant as pathogenic. Based on the evidence outlined above, the variant was classified as pathogenic. |
Baylor Genetics | RCV000552083 | SCV004215815 | pathogenic | Familial infantile myasthenia | 2024-01-10 | criteria provided, single submitter | clinical testing | |
Fulgent Genetics, |
RCV000552083 | SCV005676810 | pathogenic | Familial infantile myasthenia | 2024-01-17 | criteria provided, single submitter | clinical testing |