Total submissions: 2
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Institute of Human Genetics, |
RCV001262677 | SCV001440628 | pathogenic | Autosomal recessive early-onset Parkinson disease 23 | 2019-01-01 | criteria provided, single submitter | clinical testing | |
Laboratory for Molecular Medicine, |
RCV004017812 | SCV004847663 | likely pathogenic | Young-onset Parkinson disease | 2019-03-07 | criteria provided, single submitter | clinical testing | The p.Arg371X variant VPS13C has not been previously reported in individuals with Parkinson disease but has been identified in 2/4994 of African chromosomes by gnomAD (http://gnomad.broadinstitute.org).This nonsense variant leads to a premature termination codon at position 371, which is predicted to lead to a truncated or absent protein. Loss of function of the VPS13C gene has been recently associated with autosomal recessive early onset parkinsonism (Schormair 2018; Lesage 2016; Darvish 2018). In summary, although additional studies are required to fully establish its clinical significance, this variant meets criteria to be classified as likely pathogenic for autosomal recessive early onset parkinsonism. ACMG/AMP Criteria applied: PM2, PVS1_Strong. |