Total submissions: 6
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
ARUP Laboratories, |
RCV000756825 | SCV000884748 | likely pathogenic | not provided | 2018-04-12 | criteria provided, single submitter | clinical testing | The TRPV4 c.1412_1414delTCT; p.Phe471del variant (rs515726154, ClinVar variant ID 126464) has been detected in at least two cases of metatropic dysplasia, one of which was infantile lethal (Camacho 2010, Dai 2010). Functional studies in Xenopus oocytes demonstrated that the p.Phe471del variant, like other established pathogenic TRPV4 variants, results in a phenotype consistent with a constitutively open calcium channel compared to wild-type, and similar gain-of-function mutations have been associated with disease in other TRP channel proteins (Loukin 2011). This variant is absent from the general population databases (1000 Genomes Project, Exome Variant Server, Genome Aggregation Database), indicating it is not a common polymorphism. Based on the available information, the p.Phe471del variant is likely to be a pathogenic variant associated with metatropic dysplasia. |
Genomic Medicine Lab, |
RCV001376047 | SCV001573062 | pathogenic | Skeletal dysplasia and progressive central nervous system degeneration, lethal | 2020-03-19 | criteria provided, single submitter | clinical testing | |
Ce |
RCV000756825 | SCV001961374 | pathogenic | not provided | 2024-02-01 | criteria provided, single submitter | clinical testing | TRPV4: PS2, PM2, PS4:Moderate, PM4:Supporting, PS3:Supporting |
Labcorp Genetics |
RCV003505097 | SCV004296213 | likely pathogenic | Charcot-Marie-Tooth disease axonal type 2C | 2023-06-03 | criteria provided, single submitter | clinical testing | This variant has been observed in individuals with clinical features of metatropic dysplasia (PMID: 20425821, 20577006, 22791502). This variant is not present in population databases (gnomAD no frequency). This variant, c.1412_1414del, results in the deletion of 1 amino acid(s) of the TRPV4 protein (p.Phe471del), but otherwise preserves the integrity of the reading frame. ClinVar contains an entry for this variant (Variation ID: 126464). In summary, the currently available evidence indicates that the variant is pathogenic, but additional data are needed to prove that conclusively. Therefore, this variant has been classified as Likely Pathogenic. Experimental studies have shown that this variant affects TRPV4 function (PMID: 21573172). Algorithms developed to predict the effect of variants on protein structure and function are not available or were not evaluated for this variant. |
OMIM | RCV002279715 | SCV000025479 | pathogenic | Metatropic dysplasia | 2010-10-01 | no assertion criteria provided | literature only | |
Gene |
RCV000202564 | SCV000148019 | not provided | Skeletal dysplasia | no assertion provided | literature only |