Total submissions: 3
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Labcorp Genetics |
RCV002003162 | SCV002274670 | pathogenic | 3-methylcrotonyl-CoA carboxylase 2 deficiency | 2024-07-22 | criteria provided, single submitter | clinical testing | This sequence change replaces asparagine, which is neutral and polar, with serine, which is neutral and polar, at codon 403 of the MCCC2 protein (p.Asn403Ser). This variant is present in population databases (rs142887940, gnomAD 0.02%). This missense change has been observed in individual(s) with 3-methylcrotonyl-CoA carboxylase deficiency (Invitae). In at least one individual the data is consistent with being in trans (on the opposite chromosome) from a pathogenic variant. ClinVar contains an entry for this variant (Variation ID: 1483421). Advanced modeling of protein sequence and biophysical properties (such as structural, functional, and spatial information, amino acid conservation, physicochemical variation, residue mobility, and thermodynamic stability) performed at Invitae indicates that this missense variant is expected to disrupt MCCC2 protein function with a positive predictive value of 80%. This variant disrupts the p.Asn403 amino acid residue in MCCC2. Other variant(s) that disrupt this residue have been determined to be pathogenic (PMID: 16835865). This suggests that this residue is clinically significant, and that variants that disrupt this residue are likely to be disease-causing. For these reasons, this variant has been classified as Pathogenic. |
Gene |
RCV003227056 | SCV003923570 | likely pathogenic | not provided | 2025-01-06 | criteria provided, single submitter | clinical testing | Observed in the heterozygous state in one individual from a cohort of patients with mitochondrial complex I deficiency (PMID: 20818383); In silico analysis supports that this missense variant has a deleterious effect on protein structure/function; This variant is associated with the following publications: (PMID: 25087612, 20818383, 16835865) |
Fulgent Genetics, |
RCV002003162 | SCV005666619 | likely pathogenic | 3-methylcrotonyl-CoA carboxylase 2 deficiency | 2024-05-07 | criteria provided, single submitter | clinical testing |