Total submissions: 4
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Eurofins Ntd Llc |
RCV000153472 | SCV000202979 | uncertain significance | not provided | 2014-03-03 | criteria provided, single submitter | clinical testing | |
Labcorp Genetics |
RCV000704177 | SCV000833116 | uncertain significance | 3-methylcrotonyl-CoA carboxylase 2 deficiency | 2022-06-02 | criteria provided, single submitter | clinical testing | This sequence change replaces alanine, which is neutral and non-polar, with threonine, which is neutral and polar, at codon 160 of the MCCC2 protein (p.Ala160Thr). This variant is present in population databases (rs727504009, gnomAD 0.003%). This missense change has been observed in individual(s) with unspecified type of inborn error of metabolism (PMID: 32778825). ClinVar contains an entry for this variant (Variation ID: 167277). Advanced modeling of protein sequence and biophysical properties (such as structural, functional, and spatial information, amino acid conservation, physicochemical variation, residue mobility, and thermodynamic stability) performed at Invitae indicates that this missense variant is expected to disrupt MCCC2 protein function. In summary, the available evidence is currently insufficient to determine the role of this variant in disease. Therefore, it has been classified as a Variant of Uncertain Significance. |
Natera, |
RCV000704177 | SCV001452998 | uncertain significance | 3-methylcrotonyl-CoA carboxylase 2 deficiency | 2020-03-10 | no assertion criteria provided | clinical testing | |
Prevention |
RCV004751297 | SCV005346020 | uncertain significance | MCCC2-related disorder | 2024-07-04 | no assertion criteria provided | clinical testing | The MCCC2 c.478G>A variant is predicted to result in the amino acid substitution p.Ala160Thr. This variant was reported in a newborn screening for inborn errors of metabolism; however, clinical information was not provided (Table S5, Adhikari et al. 2020. PubMed ID: 32778825). This variant is reported in 0.0029% of alleles in individuals of Latino descent in gnomAD. A different missense variant (c.479C>A, Ala160Asp) has been reported, along with another variant of uncertain significance, in a patient with elevated C5-OH by newborn screening suggestive of 3-methylcrotonyl-CoA carboxylase deficiency with mild elevation of 3-methylcrotonylglycine and normal 3-hydroxyisovaleric acid (Cheng et al. 2023. PubMed ID: 36822454). Although we suspect this variant may be pathogenic, at this time, the clinical significance of the c.478G>A variant is uncertain due to the absence of conclusive functional and genetic evidence. |