Total submissions: 3
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Gene |
RCV000479810 | SCV000566904 | pathogenic | not provided | 2023-05-11 | criteria provided, single submitter | clinical testing | Published functional studies found p.(D222H) is associated with significantly reduced enzyme activity and protein expression (Banka et al., 2014; Huang et al., 2019); Not observed at significant frequency in large population cohorts (gnomAD); In silico analysis supports that this missense variant has a deleterious effect on protein structure/function; This variant is associated with the following publications: (PMID: 30483896, 25458521, 29269382) |
Breda Genetics srl | RCV001078175 | SCV001190339 | pathogenic | Childhood encephalopathy due to thiamine pyrophosphokinase deficiency | 2020-03-11 | criteria provided, single submitter | clinical testing | There is no information on frequency of this variant in gnomAD, 1000 Genomes or NHLI Exome Sequencing Project (ESP). The nucleotide position is conserved across 35 mammalian species (GERP RS: 4.61). This variant has been identified by Banka et al. (2014), in the homozygous state, in a patient with a non-episodic Leigh-like syndrome, with early developmental global developmental delay (PMID: 25458521). ClinVar contains an entry for this variant (Variation ID: 419232). |
Fulgent Genetics, |
RCV001078175 | SCV002812177 | likely pathogenic | Childhood encephalopathy due to thiamine pyrophosphokinase deficiency | 2022-01-17 | criteria provided, single submitter | clinical testing |