Total submissions: 4
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Revvity Omics, |
RCV000001099 | SCV003831165 | likely pathogenic | Hereditary spastic paraplegia 35 | 2022-09-06 | criteria provided, single submitter | clinical testing | |
3billion | RCV000001099 | SCV003841930 | uncertain significance | Hereditary spastic paraplegia 35 | 2023-02-23 | criteria provided, single submitter | clinical testing | The variant is not observed in the gnomAD v2.1.1 dataset. In silico tool predictions suggest damaging effect of the variant on gene or gene product (REVEL: 0.94; 3Cnet: 0.94). Same nucleotide change resulting in same amino acid change has been previously reported to be associated with FA2H -related disorder (ClinVar ID: VCV000001044 / PMID: 19068277). The variant has been reported to co-segregate with the disease in at least one similarly affected relative/individual in the same family or similarly affected unrelated family (PMID: 19068277). However, the evidence of pathogenicity is insufficient at this time. Therefore, this variant is classified as VUS according to the recommendation of ACMG/AMP guideline. |
Breakthrough Genomics, |
RCV000001099 | SCV005088805 | pathogenic | Hereditary spastic paraplegia 35 | 2020-01-30 | criteria provided, single submitter | clinical testing | This variant is predicted to be damaging by in-silico missense prediction tools (SIFT and Polyphen2). The variant was previously reported in a consanguineous Arab-Muslim family (as c.103G→T and D35Y in the article) in the homozygous state and the patient was diagnosed with Leukodystrophy with Spastic Paraparesis and Dystonia [PMID: 19068277, 21592092, 24299421]. In-vitro functional studies revealed that the cells harboring the p.Asp35Tyr variant exhibited a significant reduction in endogenous FA2H enzymatic activity when compared to wild type cells suggesting its loss-of-function [PMID: 19068277]. |
OMIM | RCV000001099 | SCV000021249 | pathogenic | Hereditary spastic paraplegia 35 | 2008-11-01 | no assertion criteria provided | literature only |