Total submissions: 1
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Pittsburgh Clinical Genomics Laboratory, |
RCV004785005 | SCV005397387 | pathogenic | Developmental and epileptic encephalopathy, 44 | 2022-04-11 | criteria provided, single submitter | clinical testing | This sequence variant is a single nucleotide deletion (delG) in exon 8 of 12 of UBA5 and results in an early termition codon 9 amino acids downstream of the frameshift at Ala236. This variant is predicted to generate a non-functiol allele through either the expression of a truncated protein, or a loss of UBA5 expression due to nonsense mediated decay. This is a novel variant that has not been previously reported to clinical variant repositories (ClinVar) and is absent from control population datasets (gnomAD 0 of ~251000 alleles). Because truncating variants are a known mechanism of disease for UBA5 (PMID: 27545681), we consider this variant to be pathogenic. ACMG Criteria: PM2, PM3, PVS1 |