Total submissions: 2
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Labcorp Genetics |
RCV001226858 | SCV001399185 | pathogenic | Familial aplasia of the vermis; Meckel-Gruber syndrome; Nephronophthisis | 2023-07-10 | criteria provided, single submitter | clinical testing | For these reasons, this variant has been classified as Pathogenic. ClinVar contains an entry for this variant (Variation ID: 954408). This premature translational stop signal has been observed in individual(s) with Leber congenital amaurosis (PMID: 20683928). This variant is present in population databases (rs770474857, gnomAD 0.0009%). This sequence change creates a premature translational stop signal (p.Leu1141Phefs*5) in the CEP290 gene. It is expected to result in an absent or disrupted protein product. Loss-of-function variants in CEP290 are known to be pathogenic (PMID: 16909394, 17345604, 20690115). |
Baylor Genetics | RCV003469397 | SCV004216632 | pathogenic | Bardet-Biedl syndrome 14 | 2023-05-31 | criteria provided, single submitter | clinical testing |