Total submissions: 3
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Gene |
RCV001585687 | SCV001812465 | likely pathogenic | not provided | 2021-06-24 | criteria provided, single submitter | clinical testing | Frameshift variant predicted to result in protein truncation as the last 48 amino acids are replaced with 60 different amino acids, although loss-of-function variants have not been reported downstream of this position in the protein; Not observed at a significant frequency in large population cohorts (Lek et al., 2016); This variant is associated with the following publications: (PMID: 30089828) |
Women's Health and Genetics/Laboratory Corporation of America, |
RCV003235379 | SCV003934032 | pathogenic | Neurodegeneration with brain iron accumulation | 2023-05-19 | criteria provided, single submitter | clinical testing | Variant summary: COASY c.1549_1550delAG (p.Ser517ProfsX61) causes a frameshift which results in an extension of the protein. The variant allele was found at a frequency of 1.2e-05 in 251012 control chromosomes (gnomAD). c.1549_1550delAG has been reported in the literature in at least one compound heterozygous individual affected with Pontocerebellar hypoplasia, microcephaly and arthrogryposis (van Dijk_2018). These data do not allow any conclusion about variant significance. Amniocytes from this compound heterozygous individual had undetectable levels of COASY protein and ~1% COASY activity compared to controls, indicating loss-of-function (van Dijk_2018). The following publication has been ascertained in the context of this evaluation (PMID: 30089828). Two ClinVar submitters have assessed the variant since 2014: one classified the variant as likely pathogenic, and one as pathogenic. Based on the evidence outlined above, the variant was classified as pathogenic. |
OMIM | RCV000735980 | SCV000864179 | pathogenic | Pontocerebellar hypoplasia, type 12 | 2019-01-09 | no assertion criteria provided | literature only |