Total submissions: 2
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Institute for Genomic Medicine |
RCV001249669 | SCV001423675 | pathogenic | Smith-Magenis syndrome | 2017-11-17 | criteria provided, single submitter | clinical testing | [ACMG/AMP: PVS1, PM2, PP3] This alteration is a null variant in a gene where LOF is a known mechanism of disease [PVS1], is absent from or rarely observed in large-scale population databases [PM2], is predicted to be damaging by multiple functional prediction tools [PP3]. |
Prevention |
RCV003393922 | SCV004119663 | likely pathogenic | RAI1-related disorder | 2023-05-05 | criteria provided, single submitter | clinical testing | The RAI1 c.4681C>T variant is predicted to result in premature protein termination (p.Arg1561*). This variant was reported in an individual with Smith-Magenis syndrome (Miller et al 2020. PubMed ID: 32371413). This variant is reported in 0.00088% of alleles in individuals of European (non-Finnish) descent in gnomAD (http://gnomad.broadinstitute.org/variant/17-17700943-C-T). Nonsense variants in RAI1 are expected to be pathogenic. This variant is interpreted as likely pathogenic. |