Total submissions: 5
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
NIHR Bioresource Rare Diseases, |
RCV000851914 | SCV000899995 | likely pathogenic | Macrothrombocytopenia | 2019-02-01 | criteria provided, single submitter | research | |
Invitae | RCV002512603 | SCV003443381 | pathogenic | not provided | 2022-05-07 | criteria provided, single submitter | clinical testing | This sequence change replaces arginine, which is basic and polar, with tryptophan, which is neutral and slightly polar, at codon 318 of the TUBB1 protein (p.Arg318Trp). This variant is present in population databases (rs121918555, gnomAD 0.06%), and has an allele count higher than expected for a pathogenic variant. This missense change has been observed in individual(s) with clinical features of TUBB1-related macrothrombocytopenia (PMID: 18849486, 31064749, 33400601). It has also been observed to segregate with disease in related individuals. ClinVar contains an entry for this variant (Variation ID: 425). Algorithms developed to predict the effect of missense changes on protein structure and function are either unavailable or do not agree on the potential impact of this missense change (SIFT: "Not Available"; PolyPhen-2: "Probably Damaging"; Align-GVGD: "Not Available"). Experimental studies have shown that this missense change affects TUBB1 function (PMID: 18849486). For these reasons, this variant has been classified as Pathogenic. |
Revvity Omics, |
RCV000000453 | SCV003816022 | likely pathogenic | Macrothrombocytopenia, isolated, 1, autosomal dominant | 2022-02-09 | criteria provided, single submitter | clinical testing | |
OMIM | RCV000000453 | SCV000020602 | pathogenic | Macrothrombocytopenia, isolated, 1, autosomal dominant | 2009-01-08 | no assertion criteria provided | literature only | |
Zotz- |
RCV000000453 | SCV004041702 | likely pathogenic | Macrothrombocytopenia, isolated, 1, autosomal dominant | 2023-10-09 | no assertion criteria provided | clinical testing |