Total submissions: 2
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Labcorp Genetics |
RCV000128840 | SCV001419140 | pathogenic | Polyglucosan body myopathy type 1 | 2019-10-12 | criteria provided, single submitter | clinical testing | This sequence change creates a premature translational stop signal (p.Gln264*) in the RBCK1 gene. It is expected to result in an absent or disrupted protein product. This variant is not present in population databases (ExAC no frequency). This variant has been observed in an family affected with progressive muscular weakness and cardiomyopathy (PMID: 23889995). This variant is also known as p.Q222X in the literature. ClinVar contains an entry for this variant (Variation ID: 140629). Loss-of-function variants in RBCK1 are known to be pathogenic (PMID:23104095, 2379848, 23889995). For these reasons, this variant has been classified as Pathogenic. |
OMIM | RCV001840049 | SCV000172496 | pathogenic | Polyglucosan body myopathy 1 without immunodeficiency | 2013-01-01 | no assertion criteria provided | literature only |