Total submissions: 1
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Pediatrics Genetics, |
RCV005230885 | SCV005848197 | uncertain significance | Neurodegeneration with brain iron accumulation 4 | 2025-02-19 | criteria provided, single submitter | clinical testing | Homozygous missense variant c.163G>T in exon 3 of C19orf12 that results in p.Gly55Trp. This variant is not reported in gnomAD and 1000G. Amino acid is conserved across species. Gene C19orf12 is causative for Neurodegeneration with brain iron accumulation 4 which shows AD/AR inheritance. PM1, PM2, PP2, and PP3. |