Total submissions: 2
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Labcorp Genetics |
RCV003066872 | SCV003447611 | pathogenic | not provided | 2022-11-19 | criteria provided, single submitter | clinical testing | For these reasons, this variant has been classified as Pathogenic. This variant has not been reported in the literature in individuals affected with PNPT1-related conditions. This variant is present in population databases (rs780383722, gnomAD 0.004%). This sequence change creates a premature translational stop signal (p.Arg132*) in the PNPT1 gene. It is expected to result in an absent or disrupted protein product. Loss-of-function variants in PNPT1 are known to be pathogenic (PMID: 28594066, 30244537). |
3billion | RCV003314052 | SCV004013797 | likely pathogenic | Combined oxidative phosphorylation defect type 13 | criteria provided, single submitter | clinical testing | The variant is observed at an extremely low frequency in the gnomAD v2.1.1 dataset (total allele frequency: <0.001%). The variant is predicted to result in a loss or disruption of normal protein function through nonsense-mediated decay (NMD) or protein truncation. Multiple pathogenic variants are reported downstream of the variant. Therefore, this variant is classified as Likely pathogenic according to the recommendation of ACMG/AMP guideline. |