Total submissions: 3
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
DASA | RCV002221703 | SCV002498801 | likely pathogenic | Spastic paraplegia 84, autosomal recessive | 2022-04-10 | criteria provided, single submitter | clinical testing | The c.1852C>T;p.(Arg618)* variant creates a premature translational stop signal in the PI4KA gene. It is expected to result in an absent or disrupted protein product -PVS1. The variant is present at low allele frequencies population databases (rs201395198 – gnomAD 0.001006%; ABraOM no frequency - http://abraom.ib.usp.br) - PM2_supporting. In summary, the currently available evidence indicates that the variant is likely pathogenic |
Prevention |
RCV004533974 | SCV004733030 | likely pathogenic | PI4KA-related disorder | 2023-12-04 | criteria provided, single submitter | clinical testing | The PI4KA c.1852C>T variant is predicted to result in premature protein termination (p.Arg618*). This variant, along with another variant in PI4KA, was reported in an individual with a neurodevelopmental syndrome with hypomyelinating leukodystrophy (Supplemental Table 1, P5, Verdura et al. 2021. PubMed ID: 34415322). This variant is reported in 0.31% of alleles in individuals of Ashkenazi Jewish descent in gnomAD. Nonsense variants in PI4KA are expected to be pathogenic. This variant is interpreted as likely pathogenic. |
Undiagnosed Diseases Network, |
RCV003164309 | SCV003915638 | uncertain significance | Phenylketonuria | 2022-11-29 | no assertion criteria provided | clinical testing |