Total submissions: 2
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Gene |
RCV002255055 | SCV002526319 | pathogenic | not provided | 2023-01-27 | criteria provided, single submitter | clinical testing | Nonsense variant predicted to result in protein truncation or nonsense mediated decay in a gene for which loss-of-function is a known mechanism of disease; Not observed in large population cohorts (gnomAD); Has not been previously published as pathogenic or benign to our knowledge |
Division of Pediatric Neurology, |
RCV003492745 | SCV004239112 | likely pathogenic | Intellectual disability-cardiac anomalies-short stature-joint laxity syndrome | no assertion criteria provided | clinical testing | The de novo heterozygous c.1123C>T, (p.Gln375Ter) variant was absent from healthy population databases (gnomAD v.3.1.2). This variant likely results in reduced protein expression. This variant was found in a patient with a phenotype that is associated to PUF60-related disorders (neurodevelopmental disorder, short stature, skin abnormalities, craniofacial dysmorphia). A previous study has reported a similar phenotype with a frameshift-truncating variant located closely to this variant (Fennell et al., 2022). |