Total submissions: 1
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Rady Children's Institute for Genomic Medicine, |
RCV000853262 | SCV000996089 | pathogenic | Optic atrophy with or without deafness, ophthalmoplegia, myopathy, ataxia, and neuropathy | 2017-12-13 | criteria provided, single submitter | clinical testing | This canonical splice donor variant is predicted to alter the function of the protein. This variant is absent from population databases, thus it is presumed to be rare. The genomic position is highly conserved and in silico splicing algorithms predict the variant alters splicing mechanisms. Although this variant has not been previously reported in the literature to our knowledge, a similar pathogenic splice site variant located adjacent (c.556+2T>G) has been previously reported and splice site variants are well established as disease causing in the OPA1 gene (PMID: 26867657). Based on the combined evidence, the c.556+1G>A variant is classified as pathogenic. |