Total submissions: 1
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
3billion | RCV001775336 | SCV002012140 | likely pathogenic | Encephalopathy, progressive, early-onset, with brain edema and/or leukoencephalopathy, 1 | 2021-10-02 | criteria provided, single submitter | clinical testing | It is not observed in the gnomAD v2.1.1 dataset (PM2). The variant was observed in trans with a pathogenic variant (NM_144772.2: c.229del) as compound heterozygous (3billion dataset, PM3). The variant has been reported to co-segregate with the disease in at least one similarly affected relative/individual in the same family (3billion dataset, PP1). In silico tool predictions suggest damaging effect of the variant on gene or gene product (REVEL: 0.802, PP3). Therefore, this variant is classified as likely pathogenic according to the recommendation of ACMG/AMP guideline. |