Total submissions: 2
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Ambry Genetics | RCV000622298 | SCV000740945 | pathogenic | Inborn genetic diseases | 2015-06-03 | criteria provided, single submitter | clinical testing | |
Labcorp Genetics |
RCV001047167 | SCV001211104 | pathogenic | Dystonia 12 | 2022-08-22 | criteria provided, single submitter | clinical testing | This sequence change replaces leucine, which is neutral and non-polar, with proline, which is neutral and non-polar, at codon 924 of the ATP1A3 protein (p.Leu924Pro). This variant is not present in population databases (gnomAD no frequency). This missense change has been observed in individual(s) with ATP1A3-related conditions (PMID: 31425744, 31618474). In at least one individual the variant was observed to be de novo. ClinVar contains an entry for this variant (Variation ID: 520712). Advanced modeling of protein sequence and biophysical properties (such as structural, functional, and spatial information, amino acid conservation, physicochemical variation, residue mobility, and thermodynamic stability) performed at Invitae indicates that this missense variant is expected to disrupt ATP1A3 protein function. Experimental studies have shown that this missense change affects ATP1A3 function (PMID: 31425744). For these reasons, this variant has been classified as Pathogenic. |