Total submissions: 6
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Gene |
RCV000255734 | SCV000322116 | pathogenic | not provided | 2018-11-30 | criteria provided, single submitter | clinical testing | The R639X pathogenic variant in the VPS13B gene has been reported previously in a patient with Cohen syndrome including features of microcephaly, short stature, and truncal obesity. This individual was presumed compound heterozygous for this pathogenic variant and another protein truncating/loss-of-function variant; this patient also harbored a pathogenic variant in the ELANE gene, which was felt to be related to her severe neutropenia (Beene et al., 2015). The R639X variant is predicted to cause loss of normal protein function either through protein truncation or nonsense-mediated mRNA decay. The R639X variant was not observed in approximately 6500 individuals of European and African American ancestry in the NHLBI Exome Sequencing Project, indicating it is not a common benign variant in these populations. We interpret R639X as a pathogenic variant. |
Eurofins Ntd Llc |
RCV000255734 | SCV000703985 | pathogenic | not provided | 2016-12-12 | criteria provided, single submitter | clinical testing | |
Equipe Genetique des Anomalies du Developpement, |
RCV000824874 | SCV000965781 | likely pathogenic | Cohen syndrome | 2016-01-04 | criteria provided, single submitter | clinical testing | |
Invitae | RCV000824874 | SCV002231527 | pathogenic | Cohen syndrome | 2024-01-04 | criteria provided, single submitter | clinical testing | This sequence change creates a premature translational stop signal (p.Arg639*) in the VPS13B gene. It is expected to result in an absent or disrupted protein product. Loss-of-function variants in VPS13B are known to be pathogenic (PMID: 15141358, 16648375, 20461111). This variant is present in population databases (rs764776104, gnomAD 0.003%). This premature translational stop signal has been observed in individual(s) with clinical features of Cohen syndrome (PMID: 28559085). ClinVar contains an entry for this variant (Variation ID: 265334). For these reasons, this variant has been classified as Pathogenic. |
Counsyl | RCV000824874 | SCV001132510 | likely pathogenic | Cohen syndrome | 2015-08-20 | no assertion criteria provided | clinical testing | |
Natera, |
RCV000824874 | SCV001454810 | pathogenic | Cohen syndrome | 2020-09-16 | no assertion criteria provided | clinical testing |