Total submissions: 4
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Labcorp Genetics |
RCV000692736 | SCV000820576 | pathogenic | Nephronophthisis | 2023-10-20 | criteria provided, single submitter | clinical testing | This sequence change creates a premature translational stop signal (p.Gln855*) in the NPHP3 gene. It is expected to result in an absent or disrupted protein product. Loss-of-function variants in NPHP3 are known to be pathogenic (PMID: 18371931, 23559409). This variant is present in population databases (rs201237799, gnomAD 0.009%). This premature translational stop signal has been observed in individual(s) with infantile nephronophthisis (PMID: 19177160). ClinVar contains an entry for this variant (Variation ID: 571559). For these reasons, this variant has been classified as Pathogenic. |
Gene |
RCV001561432 | SCV001784038 | likely pathogenic | not provided | 2023-06-28 | criteria provided, single submitter | clinical testing | Identified in an individual with nephronophthisis who also harbored a second variant in NPHP3 (Tory et al., 2009); Nonsense variant predicted to result in protein truncation or nonsense mediated decay in a gene for which loss-of-function is a known mechanism of disease; Not observed at a significant frequency in large population cohorts (gnomAD); This variant is associated with the following publications: (PMID: 25525159, 31980526, 36090483, 31345219, 19177160) |
Fulgent Genetics, |
RCV002485656 | SCV002793886 | likely pathogenic | Renal-hepatic-pancreatic dysplasia 1; Nephronophthisis 3; NPHP3-related Meckel-like syndrome | 2022-04-08 | criteria provided, single submitter | clinical testing | |
Johns Hopkins Genomics, |
RCV003485630 | SCV004239066 | pathogenic | NPHP3-related Meckel-like syndrome | 2023-10-06 | criteria provided, single submitter | clinical testing | NPHP3 c.2563C>T has been reported in the compound heterozygous state in at least one patient with nephronophthisis, and has also been reported in ClinVar (Variation ID 571559). This variant (rs201237799) is rare (<0.1%) in a large population dataset (gnomAD v2.1.1: 11/282752 total alleles; 0.004%; no homozygotes). This nonsense variant results in a premature stop codon in exon 18 of 27, likely leading to nonsense-mediated decay and lack of protein production. We consider c.2563C>T in NPHP3 to be pathogenic. |