Total submissions: 4
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Labcorp Genetics |
RCV001939549 | SCV002233131 | pathogenic | Nephronophthisis | 2021-10-31 | criteria provided, single submitter | clinical testing | This variant is present in population databases (rs773760404, gnomAD 0.03%). For these reasons, this variant has been classified as Pathogenic. This variant has not been reported in the literature in individuals affected with NPHP3-related conditions. This sequence change creates a premature translational stop signal (p.Arg157Glufs*31) in the NPHP3 gene. It is expected to result in an absent or disrupted protein product. Loss-of-function variants in NPHP3 are known to be pathogenic (PMID: 18371931, 23559409). |
Fulgent Genetics, |
RCV002497873 | SCV002806398 | likely pathogenic | Renal-hepatic-pancreatic dysplasia 1; Nephronophthisis 3; NPHP3-related Meckel-like syndrome | 2024-05-13 | criteria provided, single submitter | clinical testing | |
Johns Hopkins Genomics, |
RCV003485752 | SCV004239067 | pathogenic | NPHP3-related Meckel-like syndrome | 2023-10-06 | criteria provided, single submitter | clinical testing | This NPHP3 variant (rs773760404) is rare (<0.1%) in a large population dataset (gnomAD v3.1.2: 3/151942 total alleles; 0.002%; no homozygotes). It has been reported in ClinVar (Variation ID 1454636), but has not been reported in the literature, to our knowledge. This frameshift variant results in a premature stop codon in exon 3 of 27, likely leading to nonsense-mediated decay and lack of protein production. We consider c.469del in NPHP3 to be pathogenic. |
Prevention |
RCV004741167 | SCV005348113 | likely pathogenic | NPHP3-related disorder | 2024-04-19 | no assertion criteria provided | clinical testing | The NPHP3 c.469delA variant is predicted to result in a frameshift and premature protein termination (p.Arg157Glufs*31). This variant has been reported in a cohort study about retinal diseases (Hanany et al. 2020. PubMed ID: 31964843. Table S3). This variant is reported in 0.00089% of alleles in individuals of European (Non-Finnish) descent in gnomAD. Frameshift variants in NPHP3 are expected to be pathogenic. This variant is interpreted as likely pathogenic. |