Total submissions: 2
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Clin |
RCV003993724 | SCV004812235 | likely pathogenic | Monogenic diabetes | 2024-04-05 | reviewed by expert panel | curation | The c.124G>A variant in the hepatocyte nuclear factor 4-alpha gene, HNF4A, causes an amino acid change of glycine to arginine at codon 42 (p.(Gly42Arg)) of NM_175914.5. This variant is located within the DNA binding domain (codons 37-113) of HNF4A, which is defined as crucial for the protein's function by the ClinGen MDEP (PM1_Supporting). This variant is also predicted to be deleterious by computational evidence, with a REVEL score of 0.948, which is greater than the MDEP VCEP threshold of 0.70 (PP3). This variant has an incomputable gnomAD v2.1.1 Popmax filtering allele frequency due to 1 copy in the European non-Finnish subpopulation and zero copies in any other subpopulation, thereby meeting the ClinGen MDEP threshold criteria for PM2_Supporting (ENF Popmax FAF <= 0.000003 and <= 2 copies in ENF and <=1 copy in any other subpopulation) (PM2_Supporting). This variant was identified in seven unrelated individuals with non-autoimmune and non-absolute/near-absolute insulin-deficient diabetes (PS4; PMID: 26552609, internal lab contributors). However, the MODY probability is either unable to be calculated due to lack of clinical information or the calculated MODY probability is <50% (PMID:26552609, internal lab contributors). This variant segregated with diabetes, with three informative meioses in one family with MODY (PP1; PMID:26552609). In summary, c.124G>A meets the criteria to be classified as likely pathogenic for monogenic diabetes. ACMG/AMP criteria applied, as specified by the ClinGen MDEP (specification version 2.0.0, approved 10/11/2023): PS4, PP1, PP3, PM1_Supporting, PM2_Supporting. |
Fulgent Genetics, |
RCV005030371 | SCV005656960 | likely pathogenic | Maturity-onset diabetes of the young type 1; Type 2 diabetes mellitus; Fanconi renotubular syndrome 4 with maturity-onset diabetes of the young | 2024-05-10 | criteria provided, single submitter | clinical testing |