Total submissions: 3
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Clin |
RCV003481037 | SCV004223884 | uncertain significance | Monogenic diabetes | 2023-12-25 | reviewed by expert panel | curation | The c.589C>A variant in the hepatic nuclear factor 4-alpha gene, HNF4A, causes an amino acid change of leucine to methionine at codon 197 (p.(Leu197Met)) of NM_175914.5. This variant is located within the ligand-binding domain (codons 180-220 and 300-350) of HNF4A, which is defined as critical for the protein’s function by the ClinGen MDEP (PM1_Supporting). This variant is predicted to be deleterious by computational evidence, with a REVEL score of 0.9029, which is greater than the MDEP VCEP threshold of 0.70 (PP3). This variant is absent from gnomAD v2.1.1 (PM2_Supporting). In summary, c.589C>A meets the criteria to be classified as a variant of uncertain significance for monogenic diabetes. ACMG/AMP criteria applied, as specified by the ClinGen MDEP (specification version 2.0.0, approved 10/11/2023): PP3, PM1_Supporting, PM2_Supporting. |
Broad Center for Mendelian Genomics, |
RCV001248997 | SCV001422841 | uncertain significance | Maturity-onset diabetes of the young type 1 | 2020-01-22 | criteria provided, single submitter | curation | The p.Leu219Met variant in HNF4A has not been previously reported in individuals with MODY and was absent from large population studies. Computational prediction tools and conservation analyses suggest that this variant may impact the protein, though this information is not predictive enough to determine pathogenicity. p.Leu219Met is located in a region of HNF4A that is essential to protein folding and stability, suggesting that this variant is in a functional domain and supports pathogenicity (PMID: 15123688, 15826954). In summary, while there is some suspicion for a pathogenic role, the clinical significance of this variant is uncertain. ACMG/AMP Criteria applied: PM2, PM1, PP3 (Richards 2015). |
Genetics and Molecular Pathology, |
RCV002272431 | SCV002556830 | likely pathogenic | Fanconi renotubular syndrome 4 with maturity-onset diabetes of the young | 2021-05-14 | criteria provided, single submitter | clinical testing |