Total submissions: 2
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Labcorp Genetics |
RCV000855531 | SCV004626860 | pathogenic | Multiple congenital anomalies-hypotonia-seizures syndrome 1 | 2024-01-16 | criteria provided, single submitter | clinical testing | This sequence change creates a premature translational stop signal (p.Phe597Serfs*11) in the PIGN gene. It is expected to result in an absent or disrupted protein product. Loss-of-function variants in PIGN are known to be pathogenic (PMID: 24253414, 27038415). This variant is not present in population databases (gnomAD no frequency). This premature translational stop signal has been observed in individual(s) with clinical features of PIGN-congenital disorder of glycosylation (PMID: 35179230). ClinVar contains an entry for this variant (Variation ID: 694261). For these reasons, this variant has been classified as Pathogenic. |
Institute of Human Genetics, |
RCV000855531 | SCV000998748 | likely pathogenic | Multiple congenital anomalies-hypotonia-seizures syndrome 1 | no assertion criteria provided | clinical testing |