Total submissions: 5
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Labcorp Genetics |
RCV000629460 | SCV000750403 | pathogenic | Primary ciliary dyskinesia | 2024-12-30 | criteria provided, single submitter | clinical testing | This sequence change creates a premature translational stop signal (p.Gly434Profs*4) in the DNAAF1 gene. It is expected to result in an absent or disrupted protein product. Loss-of-function variants in DNAAF1 are known to be pathogenic (PMID: 19944400, 19944405). This variant is present in population databases (rs745495583, gnomAD 0.006%). This premature translational stop signal has been observed in individual(s) with primary ciliary dyskinesia (PMID: 19944405). ClinVar contains an entry for this variant (Variation ID: 525404). For these reasons, this variant has been classified as Pathogenic. |
Ambry Genetics | RCV000629460 | SCV002692478 | pathogenic | Primary ciliary dyskinesia | 2021-08-24 | criteria provided, single submitter | clinical testing | The c.1300_1322del23 pathogenic mutation, located in coding exon 8 of the DNAAF1 gene, results from a deletion of 23 nucleotides at nucleotide positions 1300 to 1322, causing a translational frameshift with a predicted alternate stop codon (p.G434Pfs*4). This alteration was detected along with another DNAAF1 translational frameshift mutation in an individual with primary ciliary dyskinesia (PCD) (Duquesnoy P et al. Am J Hum Genet, 2009 Dec;85:890-6). This alteration is expected to result in loss of function by premature protein truncation or nonsense-mediated mRNA decay. As such, this alteration is interpreted as a disease-causing mutation. |
Fulgent Genetics, |
RCV002492940 | SCV002802778 | likely pathogenic | Primary ciliary dyskinesia 13 | 2023-12-29 | criteria provided, single submitter | clinical testing | |
Gene |
RCV005255610 | SCV005908745 | pathogenic | not provided | 2024-10-08 | criteria provided, single submitter | clinical testing | Frameshift variant predicted to result in protein truncation or nonsense mediated decay in a gene for which loss of function is a known mechanism of disease; This variant is associated with the following publications: (PMID: 19944400, 19944405, Carretero-Vilarroig2024[casereport], 27996046) |
Prevention |
RCV003935743 | SCV004751027 | likely pathogenic | DNAAF1-related disorder | 2024-01-12 | no assertion criteria provided | clinical testing | The DNAAF1 c.1300_1322del23 variant is predicted to result in a frameshift and premature protein termination (p.Gly434Profs*4). This variant has been reported with a second DNAAF1 variant in an individual with primary ciliary dyskinesia (Duquesnoy et al. 2009. PubMed ID: 19944405) and in the heterozygous state in an individual with testicular cancer (Litchfield et al. 2016. PubMed ID: 27996046). At PreventionGenetics, this variant has been detected in the homozygous state in individuals who received testing for ciliopathies (Internal Data). This variant is reported in 0.0062% of alleles in individuals of European (non-Finnish) descent in gnomAD. Frameshift variants in DNAAF1 are expected to be pathogenic. This variant is interpreted as likely pathogenic. |