Total submissions: 5
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Labcorp Genetics |
RCV000002786 | SCV001576749 | pathogenic | Multiple sulfatase deficiency | 2024-11-12 | criteria provided, single submitter | clinical testing | This sequence change replaces arginine, which is basic and polar, with glutamine, which is neutral and polar, at codon 349 of the SUMF1 protein (p.Arg349Gln). This variant is present in population databases (rs137852847, gnomAD 0.0009%). This missense change has been observed in individual(s) with multiple sulfatase deficiency (PMID: 12757705). ClinVar contains an entry for this variant (Variation ID: 2667). Invitae Evidence Modeling of protein sequence and biophysical properties (such as structural, functional, and spatial information, amino acid conservation, physicochemical variation, residue mobility, and thermodynamic stability) indicates that this missense variant is expected to disrupt SUMF1 protein function with a positive predictive value of 95%. This variant disrupts the p.Arg349 amino acid residue in SUMF1. Other variant(s) that disrupt this residue have been determined to be pathogenic (PMID: 12757706, 15146462, 25373814). This suggests that this residue is clinically significant, and that variants that disrupt this residue are likely to be disease-causing. For these reasons, this variant has been classified as Pathogenic. |
Gene |
RCV002243616 | SCV002513150 | likely pathogenic | not provided | 2022-05-02 | criteria provided, single submitter | clinical testing | Published functional studies demonstrate a damaging effect showing reduced activation of sulfatases ARSA, ARSC, and ARSE compared to wild type SUMF1 (Cosma et al., 2004); Identified in a patient with severe multiple sulphatase deficiency in published literature (Cosma et al., 2003); Not observed at significant frequency in large population cohorts (gnomAD); In silico analysis supports that this missense variant has a deleterious effect on protein structure/function; This variant is associated with the following publications: (PMID: 12757706, 24484558, 28452122, 31589614, 15146462, 12757705, 18157819, 29048999, 25373814) |
Fulgent Genetics, |
RCV000002786 | SCV005664533 | likely pathogenic | Multiple sulfatase deficiency | 2024-02-25 | criteria provided, single submitter | clinical testing | |
OMIM | RCV000002786 | SCV000022944 | pathogenic | Multiple sulfatase deficiency | 2003-05-16 | no assertion criteria provided | literature only | |
Natera, |
RCV000002786 | SCV002079159 | likely pathogenic | Multiple sulfatase deficiency | 2020-07-23 | no assertion criteria provided | clinical testing |