Total submissions: 1
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Diagnostics Services |
RCV003236687 | SCV003935158 | likely pathogenic | Emery-Dreifuss muscular dystrophy 5, autosomal dominant | 2023-06-22 | criteria provided, single submitter | clinical testing | The c.990_990+4del variant is not present in publicly available population databases like 1000 Genomes, ExAC, EVS, gnomAD, Indian Exome Database or our in-house exome database. This variant has neither been published in literature nor reported to clinical databases like ClinVar, Human Gene Mutation Database (HGMD) or OMIM, in any affected individuals. In-silico pathogenicity prediction programs like MutationTaster2, CADD, Varsome, Franklin etc predicted this variant to be likely deleterious. This variant causes loss of exon-intron donor splice-junction and is predicted to affect splicing of mRNA by the activation of a cryptic donor site. |