Total submissions: 1
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Center for Genomic Medicine, |
RCV004765430 | SCV005375266 | likely pathogenic | Griscelli syndrome type 2 | 2024-10-13 | criteria provided, single submitter | clinical testing | This sequence change creates a premature translational stop signal (GRCh38; NM_004580.5:c.514C>T:p.Gln172Ter) in the RAB27A protein. This alteration is expected to result in loss of function by premature termination codon resulting in protein truncation, or nonsense-mediated mRNA decay. This alteration is interpreted as disease-causing mutation, a commonly known mechanism for disease. To our knowledge this variant not been previously curated or reported in public Database. Not observed at significant frequency in large population cohorts (gnomAD). In-silico analysis supports that this nonsense variant is pathogenic. This alteration is interpreted as disease-causing mutation, a commonly known mechanism for disease. In summary, this variant meets our criteria to be classified as Likely pathogenic for Griscelli syndrome in an autosomal recessive manner based the evidence outlined. |