Total submissions: 5
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Labcorp Genetics |
RCV002513176 | SCV001205214 | uncertain significance | Dyskeratosis congenita, autosomal dominant 2; Idiopathic Pulmonary Fibrosis | 2023-07-10 | criteria provided, single submitter | clinical testing | This sequence change replaces arginine, which is basic and polar, with cysteine, which is neutral and slightly polar, at codon 811 of the TERT protein (p.Arg811Cys). This variant is present in population databases (rs199422301, gnomAD 0.0008%). This missense change has been observed in individual(s) with dyskeratosis congenita in the homozygous state and/or familial pulmonary fibrosis in the heterozygous state (PMID: 17785587, 28192371). ClinVar contains an entry for this variant (Variation ID: 29900). Advanced modeling of protein sequence and biophysical properties (such as structural, functional, and spatial information, amino acid conservation, physicochemical variation, residue mobility, and thermodynamic stability) performed at Invitae indicates that this missense variant is expected to disrupt TERT protein function. Experimental studies have shown that this missense change affects TERT function (PMID: 17785587, 26887940). In summary, the available evidence is currently insufficient to determine the role of this variant in disease. Therefore, it has been classified as a Variant of Uncertain Significance. |
Gene |
RCV001797047 | SCV002038816 | likely pathogenic | not provided | 2021-08-11 | criteria provided, single submitter | clinical testing | Published functional studies demonstrate a damaging effect as this variant was defective in binding to telomeres, resulting in uncapping and higher apoptosis, and showing a 50% reduction in telomerase activity in transfected cells (Chu et al., 2016; Marrone et al., 2007).; In silico analysis supports that this missense variant has a deleterious effect on protein structure/function; This variant is associated with the following publications: (PMID: 17785587, 26887940, 23538340, 23716176, 29691679, 26581521, 20301779, 28192371) |
3billion | RCV002051796 | SCV002318673 | uncertain significance | Dyskeratosis congenita, autosomal dominant 2 | 2022-03-22 | criteria provided, single submitter | clinical testing | The variant is observed at an extremely low frequency in the gnomAD v2.1.1 dataset (total allele frequency: 0.000004). A missense variant is a common mechanism. Therefore, this variant is classified as uncertain significance according to the recommendation of ACMG/AMP guideline. |
OMIM | RCV000022784 | SCV000044073 | pathogenic | Autosomal recessive dyskeratosis congenita 4 | 2007-12-15 | no assertion criteria provided | literature only | |
Gene |
RCV000032383 | SCV000056039 | not provided | Dyskeratosis congenita, autosomal recessive 1 | no assertion provided | literature only |