Total submissions: 2
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Revvity Omics, |
RCV001783312 | SCV002023758 | pathogenic | Congenital myasthenic syndrome 8 | 2021-11-09 | criteria provided, single submitter | clinical testing | |
Labcorp Genetics |
RCV001783312 | SCV005770094 | pathogenic | Congenital myasthenic syndrome 8 | 2024-08-02 | criteria provided, single submitter | clinical testing | This sequence change creates a premature translational stop signal (p.Gln1406Argfs*29) in the AGRN gene. It is expected to result in an absent or disrupted protein product. Loss-of-function variants in AGRN are known to be pathogenic (PMID: 24951643). This variant is present in population databases (rs770470615, gnomAD 0.007%). This premature translational stop signal has been observed in individual(s) with arthrogryposis multiplex congenita (PMID: 33820833). ClinVar contains an entry for this variant (Variation ID: 1322937). For these reasons, this variant has been classified as Pathogenic. |