Total submissions: 2
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Labcorp Genetics |
RCV001390795 | SCV001592642 | pathogenic | Retinitis pigmentosa 12; Leber congenital amaurosis 8 | 2023-06-03 | criteria provided, single submitter | clinical testing | This variant is not present in population databases (gnomAD no frequency). This sequence change creates a premature translational stop signal (p.Leu538Profs*14) in the CRB1 gene. It is expected to result in an absent or disrupted protein product. Loss-of-function variants in CRB1 are known to be pathogenic (PMID: 10508521, 22065545, 23379534, 25412400, 26957898, 28041643, 29391521). This premature translational stop signal has been observed in individual(s) with early-onset retinal disease and Leber congenital amaurosis (PMID: 27208204). ClinVar contains an entry for this variant (Variation ID: 236470). For these reasons, this variant has been classified as Pathogenic. |
Centre for Genomic Medicine, |
RCV000225570 | SCV000282576 | likely pathogenic | Retinal dystrophy | no assertion criteria provided | clinical testing |