Total submissions: 4
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Myeli |
RCV000788035 | SCV000924610 | pathogenic | Hypomyelinating leukodystrophy 11 | criteria provided, single submitter | research | ||
Fulgent Genetics, |
RCV002487617 | SCV002791382 | pathogenic | Treacher Collins syndrome 3; Hypomyelinating leukodystrophy 11 | 2022-01-14 | criteria provided, single submitter | clinical testing | |
Labcorp Genetics |
RCV003727826 | SCV004535416 | pathogenic | not provided | 2023-08-18 | criteria provided, single submitter | clinical testing | For these reasons, this variant has been classified as Pathogenic. Algorithms developed to predict the effect of sequence changes on RNA splicing suggest that this variant may create or strengthen a splice site. ClinVar contains an entry for this variant (Variation ID: 635151). This premature translational stop signal has been observed in individual(s) with leukodystrophy and/or Treacher Collins syndrome (PMID: 30957429, 32042905). In at least one individual the data is consistent with being in trans (on the opposite chromosome) from a pathogenic variant. It has also been observed to segregate with disease in related individuals. This variant is present in population databases (rs767639108, gnomAD 0.004%). This sequence change creates a premature translational stop signal (p.Tyr306Leufs*4) in the POLR1C gene. While this is not anticipated to result in nonsense mediated decay, it is expected to disrupt the last 41 amino acid(s) of the POLR1C protein. |
Gene |
RCV003727826 | SCV005327835 | likely pathogenic | not provided | 2023-07-25 | criteria provided, single submitter | clinical testing | Frameshift variant predicted to result in protein truncation or nonsense mediated decay in a gene for which loss of function is a known mechanism of disease; This variant is associated with the following publications: (PMID: 34426522, 610060, 30957429, 33149276, 32042905) |