Total submissions: 5
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Counsyl | RCV000668857 | SCV000793530 | likely pathogenic | Usher syndrome type 2A; Retinitis pigmentosa 39 | 2017-08-24 | criteria provided, single submitter | clinical testing | |
Labcorp Genetics |
RCV001054302 | SCV001218610 | pathogenic | not provided | 2023-11-27 | criteria provided, single submitter | clinical testing | This sequence change affects a donor splice site in intron 3 of the USH2A gene. It is expected to disrupt RNA splicing. Variants that disrupt the donor or acceptor splice site typically lead to a loss of protein function (PMID: 16199547), and loss-of-function variants in USH2A are known to be pathogenic (PMID: 10729113, 10909849, 20507924, 25649381). This variant is not present in population databases (gnomAD no frequency). Disruption of this splice site has been observed in individuals with Usher syndrome (PMID: 22135276, 34948090). ClinVar contains an entry for this variant (Variation ID: 553412). Algorithms developed to predict the effect of sequence changes on RNA splicing suggest that this variant may disrupt the consensus splice site. For these reasons, this variant has been classified as Pathogenic. |
Women's Health and Genetics/Laboratory Corporation of America, |
RCV001526995 | SCV001737798 | likely pathogenic | Usher syndrome | 2023-07-19 | criteria provided, single submitter | clinical testing | Variant summary: USH2A c.651+1G>A is located in a canonical splice-site and is predicted to affect mRNA splicing resulting in a significantly altered protein due to either exon skipping, shortening, or inclusion of intronic material. Several computational tools predict a significant impact on normal splicing: Four predict the variant abolishes a 5' splicing donor site. However, these predictions have yet to be confirmed by functional studies. The variant was absent in 250564 control chromosomes. c.651+1G>A has been reported in the literature in compound heterozygous individuals affected with Usher Syndrome (e.g. Stabej_2012, Mansard_2021). These data indicate that the variant may be associated with disease. To our knowledge, no experimental evidence demonstrating an impact on protein function has been reported. The following publications have been ascertained in the context of this evaluation (PMID: 34948090, 22135276). Two submitters have cited clinical-significance assessments for this variant to ClinVar after 2014. All submitters classified the variant as likely pathogenic. Based on the evidence outlined above, the variant was classified as likely pathogenic. |
Genome- |
RCV003446302 | SCV004172220 | likely pathogenic | Retinitis pigmentosa 39 | 2023-04-11 | criteria provided, single submitter | clinical testing | |
Genome- |
RCV003446301 | SCV004172221 | likely pathogenic | Usher syndrome type 2A | 2023-04-11 | criteria provided, single submitter | clinical testing |