Total submissions: 2
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Institut de Recherche Interdisciplinaire en Biologie Humaine et Moleculaire, |
RCV001007660 | SCV000998522 | likely pathogenic | DNA ligase IV deficiency | criteria provided, single submitter | clinical testing | ||
Labcorp Genetics |
RCV001007660 | SCV004538961 | likely pathogenic | DNA ligase IV deficiency | 2022-10-23 | criteria provided, single submitter | clinical testing | This sequence change replaces lysine, which is basic and polar, with glutamic acid, which is acidic and polar, at codon 283 of the LIG4 protein (p.Lys283Glu). This variant is not present in population databases (gnomAD no frequency). This missense change has been observed in individual(s) with clinical features of severe combined immunodeficiency (PMID: 28039949, 29146883, 31696992). In at least one individual the data is consistent with being in trans (on the opposite chromosome) from a pathogenic variant. ClinVar contains an entry for this variant (Variation ID: 694006). Advanced modeling of protein sequence and biophysical properties (such as structural, functional, and spatial information, amino acid conservation, physicochemical variation, residue mobility, and thermodynamic stability) performed at Invitae indicates that this missense variant is expected to disrupt LIG4 protein function. In summary, the currently available evidence indicates that the variant is pathogenic, but additional data are needed to prove that conclusively. Therefore, this variant has been classified as Likely Pathogenic. |